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Acadia Pharmaceuticals USD 4.53B 199M 2026-08
Alnylam Pharmaceuticals USD 40.19B 3.96B 2026-06
BioCryst Pharmaceuticals USD 1.9B 643M 2026-08
BioMarin Pharmaceutical USD 11.71B 651M 2026-08
Immunic USD 64M 23M 2025-12
Insmed USD 19.68B 3.43B 2026-08
Ionis Pharmaceuticals USD 13.1B 642M 2026-06
Karyopharm Therapeutics USD 221M 95M 2026-08
Kyowa Hakko Kirin JPY 1.36T 4.73B 2026-06
MacroGenics USD 184M 82M 2026-03
Neurocrine Biosciences USD 16.95B 3.7B 2026-06
Regeneron Pharmaceuticals USD 65.37B 16.31B 2026-06
Sarepta Therapeutics USD 1.5B 402M 2026-08
Ultragenyx Pharmaceutical USD 2.12B 1.16B 2026-08
Vertex Pharmaceuticals USD 137.33B 11.26B 2026-08