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Acadia Pharmaceuticals USD 4.52B 919M 2025-12
Agios Pharmaceuticals USD 2.01B 423M 2026-03
Alnylam Pharmaceuticals USD 44.15B 8.39B 2026-03
BioCryst Pharmaceuticals USD 1.66B 64M 2025-12
BioMarin Pharmaceutical USD 10.57B 290M 2026-05
Esperion Therapeutics USD 885M 351M 2025-12
Immunic USD 64M 23M 2025-12
Insmed USD 37.12B 6.68B 2025-12
Ionis Pharmaceuticals USD 12.46B 356M 2026-03
Karyopharm Therapeutics USD 956M 821M 2026-05
Kyowa Hakko Kirin JPY 1.33T 120.11B 2025-12
MacroGenics USD 102M 4M 2025-12
Moderna USD 20.15B 8.53B 2026-03
Neurocrine Biosciences USD 13.34B 800M 2026-05
PTC Therapeutics USD 6.1B 1.22B 2025-12
Regeneron Pharmaceuticals USD 81.68B 560M 2026-03
Sarepta Therapeutics USD 2.26B 238M 2025-12
Ultragenyx Pharmaceutical USD 2.04B 176M 2026-05
Vertex Pharmaceuticals USD 111.03B 2.55B 2026-05